Middle
Illness focus space*
Location
Contact
Boston Kids’s Hospital Gene Remedy Program
beta thalassemia
hemophilia A and B
ornithine transcarbamylase (OTC) deficiency
X-linked severe combined immunodeficiency (SCID-X1)
X-linked chronic granulomatous disease (X-CGD)
relapsed or treatment-resistant B-cell acute lymphoblastic leukemia (ALL)
relapsed or refractory large B-cell lymphoma
Boston Kids’s Hospital
300 Longwood Avenue, Boston MA 02115
https://www.childrenshospital.org/programs/gene-therapy-program
Cell and Gene Remedy Collaborative at CHOP
Beta thalassemia
Choroideremia
Hemophilia
Leber congenital amaurosis (LCA)
Methylmalonic acidemia
Mucopolysaccharidosis (MPS I, MPS II)
Phenylketonurias (PKU)
Sickle cell illness
Spinal muscular atrophy (SMA)
The Kids’s Hospital of Philadelphia
3501 Civic Middle Blvd
Philadelphia, PA 19104
Cell and Gene Remedy Middle at RowanSOM / Cooper Hospital
Canavan illness
Neurological problems
Rowan College, Faculty of Osteopathic Medication
2 Medical Middle Drive, Science Middle #253
Stratford, NJ 08084
P: (856) 566-6334
Middle for Cell and Gene Remedy at Baylor Faculty of Medication
AIDS
Heart problems
Baylor Faculty of Medication
One Baylor Plaza, Rm N1002
Houston, TX 77030
P: (832) 824-4670
Middle for Cell Engineering at Memorial Sloan Kettering Most cancers Middle
Blood problems
Neurologic ailments
Middle for Cell Engineering
Memorial Sloan Kettering Most cancers Middle, Field 182
1275 York Avenue
New York, NY 10065
P: (212) 639-6394
E mail: becharde@mskcc.org
Division of Genetics and Genomic Sciences at Mount Sinai
Alzheimer’s illness
Cardiovascular sickness
Crohn’s illness
Diabetes
Infectious ailments
Lysosomal storage problems
Psychiatric sicknesses
Ulcerative colitis
One Gustave L. Levy Place
Field 1498
New York, NY 10029
P: (212) 659-8542
Division of Microbiology & Molecular Genetics
Cystic fibrosis
Heart problems
College of Pittsburgh
523 Bridgeside Level II
450 Expertise Drive
Pittsburgh, PA 15219
P: (412) 648-9570
Gene Remedy Program at UPenn
Blood ailments
Eye problems
Infectious ailments
Lung ailments
Metabolic ailments
Neurologic ailments
Neuromuscular problems
Renal/liver ailments
Suite 1200 Translational Analysis Labs (TRL)
125 S. thirty first Road
Philadelphia, PA 19104
P: (215) 898-1281
Grousbeck Gene Remedy Middle
Blindness
Deafness
Neurosensory problems
Different
Gene Supply Expertise Improvement
MEE/SERI – 2W
20 Stanford Road
Boston, MA 02114
P: (617)-573-6307
Horae Gene Remedy Middle
Alpha-1 Antitrypsin Deficiency
Canavan illness
Huntington’s illness
Inherited and purchased cardiac arrhythmias
Leber congenital amaurosis (LCA)
Lou Gehrig’s illness (ALS)
Neurofibromatosis Kind 2
Retinitis pigmentosa
Stargardt illness
Tay-Sachs and Sandhoff illness
VLCAD Deficiency
UMass Medical Faculty
368 Plantation Road Worcester, MA 01605
P: (508) 856-3394
IU Faculty of Medication Brown Middle for Immunotherapy
Alzheimer’s illness
Walther Corridor
980 W. Walnut Road
Indianapolis, IN 46202
P: (317) 278-6969
Mathews Middle for Mobile Remedy
Grownup stem cell transplant
Allergy and immunology
Stable organ transplant
Northwestern Memorial Hospital
710 N. Fairbanks Court docket
Rm 7-613
Chicago, IL 60611
P: (312) 926-2210
Nationwide Kids’s Middle for Gene Remedy
Infectious Ailments
Ischemia
Lysosomal storage problems
Neuromuscular problems
Neurodegenerative ailments
Neonatal hypertension
Reperfusion damage
The Abigail Wexner Analysis Institute at Nationwide Kids’s Hospital
Analysis Bldg. II
Columbus, OH 43205
P: (614) 722-5615
Nemours Kids’s Hospital – Central Florida
- Duchenne Muscular Dystrophy
- Spinal muscular atrophy (SMA)
Nemours Kids’s Hospital
6535 Nemours Parkway, Orlando Florida 32827
https://www.nemours.org/services/neuromuscular-disorders.html
Powell Gene Remedy Middle
and
Powell Middle for Uncommon Illness Analysis
Cardiovascular ailments
Central nervous system problems
Endocrine problems
Eye ailments
Inflammatory problems
Metabolic problems
Neuromuscular problems
Pulmonary ailments
College of Florida
Tutorial Analysis Constructing Faculty of Medication
1200 Newell Drive
Gainesville, FL 32610
P: (352) 294-5171
Center for Rare Disease Research
The Vaccine and Gene Remedy Institute at OHSU
AIDS
Persistent viral infection-associated ailments
Infectious ailments
Infectious ailments of the aged
Newly rising viral ailments
Oregon Well being & Science College – West Campus
505 N.W. 185th Avenue
Beaverton, OR 97006
P: (503) 418-2700
Tulane Middle for Stem Cell Analysis & Regenerative Medication
New therapies for frequent ailments together with stroke, and a number of sclerosis
Tulane College Faculty of Medication
1430 Tulane Avenue
New Orleans, LA 70112
P: 504-988-5800
UNC Gene Remedy Middle
Eye problems
Hemophilia
Muscular dystrophies
Neurological problems (epilepsy)
Neuropathic lysosomal storage ailments (MPS and Krabbe illness)
College of North Carolina
7119 Thurston Bowles Bldg.
104 Manning Drive
Campus Field 7352
Chapel Hill, NC 27599
P: 919-962-3285
College of Iowa Gene Remedy Middle
Cystic fibrosis
Central nervous system problems
Ailments affecting muscle,
vessels, pores and skin, the liver and the lungs
Roy J. and Lucille A. Carver Faculty of Medication
451 Newton Highway
200 Medication Admin. Constructing
Iowa Metropolis, IA 52242
College of Minnesota Gene Remedy Middle
Mucopolysaccharidoses (MPS) and associated ailments
Medical Faculty Division of Pediatrics
2450 Riverside Avenue
sixth Flooring, East Constructing
Supply Code 8952A
Minneapolis, MN 55454
P: (612) 624-3113
Collagen VI myopathies
Duchenne muscular dystrophy
Leukodystrophies
Spinal Muscular Atrophy
College of Utah- Eccles Institute of Human Genetics; 15 N. 2030 E.
Salt Lake Metropolis, UT 84112
P: 801-585-9717
UT Southwestern Medical Middle
Central nervous system problems
Neurodegenerative ailments
Neuromuscular problems
Lysosomal storage problems
Metabolic problems
Genetic epilepsies
Neurodevelopmental problems
UT Southwestern Medical Middle
5323 Harry Hines Blvd.
Dallas, TX 75390
